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Back to Estimates of Funding for Various Research, Condition, and Disease Categories (RCDC) Click the column headings to sort project listings.
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CategoryFunding ICProject NumberSub Project #Project TitlePI NameOrg NameState / CountryAmount
Gene Therapy NCI 1R43CA114924-01A2 Nanoparticles for the Treatment of Lung Cancer CHADA, SUNIL INTROGEN RESEARCH INSTITUTE, INC. TX $234,382
Gene Therapy NHLBI 7K08HL071613-03 Novel Strategies for Aerosolized AAV Gene Therapy FISCHER, ANNE UNIVERSITY OF TEXAS SW MED CTR/DALLAS TX $128,250
Gene Therapy NIAID 5R01AI063142-04 Ad5 Fiber and Penton mts: Influence on immune activation FALCK-PEDERSEN, ERIK WEILL MEDICAL COLLEGE OF CORNELL UNIV NY $390,669
Gene Therapy NHLBI 1R01HL087285-01A1 Genetic Modification of Human Hematopoietic Stem Cells with Pseudotyped rAAV CHATTERJEE, SASWATI CITY OF HOPE/BECKMAN RESEARCH INSTITUTE CA $416,042
Gene Therapy NIGMS 5R01GM042539-17 Regulation of Tissue Specific Gene Expression GEYER, PAMELA UNIVERSITY OF IOWA IA $329,979
Gene Therapy NCI 5R01CA115965-02 FHIT Gene Therapy in Cancer Prevention and Treatment CROCE, CARLO OHIO STATE UNIVERSITY OH $228,000
Gene Therapy NHLBI 5K99HL088692-02 HDAd-mediated gene therapy for hemophilia B BRUNETTI-PIERRI, NICOLA BAYLOR COLLEGE OF MEDICINE TX $90,000
Gene Therapy NIDDK 5R01DK065739-05 FUNCTIONAL BIOMATERIALS FOR ANTISENSE DELIVERY TO ISLET KIM, SUNG WAN UNIVERSITY OF UTAH UT $293,812
Gene Therapy NIAID 5R01AI039416-12 Gene Transfer System for AIDS Therapy GARCIA-MARTINEZ, J. VICTOR UNIVERSITY OF TEXAS SW MED CTR/DALLAS TX $326,489
Gene Therapy NIAID 5R01AI067952-03 AAV and the DNA Damage Machinery WEITZMAN, MATTHEW SALK INSTITUTE FOR BIOLOGICAL STUDIES CA $406,787
Gene Therapy NIDDK 5R01DK048252-15 Pathophysiology of Distal Tyrosine Pathway Disorders GROMPE, MARKUS OREGON HEALTH AND SCIENCE UNIVERSITY OR $308,500
Gene Therapy NHLBI 5K08HL083095-02 Role of Calcium-Activated Chloride Channels in Airway Disease Phenotypes PATEL, ANAND WASHINGTON UNIVERSITY MO $119,718
Gene Therapy NHLBI 5R01HL076488-04 Pulmonary Transgene Expression Imaging with PET ROGERS, BUCK WASHINGTON UNIVERSITY MO $444,927
Gene Therapy NHLBI 1F32HL090350-01 SERCA2a and Cardiac Alternans: Insights from Gene Therapy CUTLER, MICHAEL METROHEALTH MEDICAL CENTER OH $52,898
Gene Therapy NCI 5R01CA101837-04 MnSOD-PL Irradiation Protection of the Oral Cavity GREENBERGER, JOEL UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $230,171
Gene Therapy NHLBI 5R01HL075713-05 OVERCOMING POSITION EFFECTS WITH CHROMATIN INSULATORS EMERY, DAVID UNIVERSITY OF WASHINGTON WA $323,425
Gene Therapy NHLBI 5R01HL079023-04 Enhancing hepatocyte gene transfer for Hemophilia A MCCRAY, PAUL UNIVERSITY OF IOWA IA $274,118
Gene Therapy NHLBI 5R01HL079370-04 Gene Delivery into Human Hematopoietic Cells BANK, ARTHUR COLUMBIA UNIVERSITY HEALTH SCIENCES NY $343,479
Gene Therapy NIDCD 5R01DC006501-05 Genetic approach for transneuronal NA circuitry mapping KIM, KWANG-SOO MC LEAN HOSPITAL (BELMONT, MA) MA $237,311
Gene Therapy NIDDK 5R01DK074026-03 Antioxidant Gene Therapy to Treat Diabetic Neuropathy GOSS, JAMES UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $315,499
Gene Therapy NIAID 5R01AI041636-11 Adenovirus as a Vector for Gene Therapy HEARING, PATRICK STATE UNIVERSITY NEW YORK STONY BROOK NY $376,408
Gene Therapy NIAID 5R01AI063340-04 Gene Therapy for Athabascan SCID MCIVOR, R UNIVERSITY OF MINNESOTA TWIN CITIES MN $306,264
Gene Therapy NINDS 5R21NS055212-02 Targeting Gene Delivery to the CNS Blood-Brain Barrier CHEN, IRVIN UNIVERSITY OF CALIFORNIA LOS ANGELES CA $202,781
Gene Therapy NIDDK 5K01DK073367-03 Targeted Integration of a Lentiviral Vector SINN, PATRICK UNIVERSITY OF IOWA IA $119,670
Gene Therapy NHLBI 5R01HL080789-03 Molecular Biology of Recombinant AAV Genomes XIAO, WEIDONG CHILDREN'S HOSPITAL OF PHILADELPHIA PA $359,939
Gene Therapy NCI 5R21CA116525-02 Design of targeted native tropism-ablated adenovirus DMITRIEV, IGOR UNIVERSITY OF ALABAMA AT BIRMINGHAM AL $145,500
Gene Therapy NCI 5R01CA042992-22 Liposome and Polycationic Gene Therapy for Osteosarcoma KLEINERMAN, EUGENIE UNIVERSITY OF TEXAS MD ANDERSON CAN CTR TX $263,918
Gene Therapy NINDS 5R01NS034568-13 STRATEGIES TO ENHANCE GENE TRANSFER TO THE CNS DAVIDSON, BEVERLY UNIVERSITY OF IOWA IA $323,419
Gene Therapy NIAID 7R01AI072773-02 Transduction of Schistosoma mansoni by pseudotyped retrovirus BRINDLEY, PAUL GEORGE WASHINGTON UNIVERSITY DC $448,408
Gene Therapy NINDS 5R01NS048441-04 Development of therapies to retard Parkinson's disease YAGI, TAKAO SCRIPPS RESEARCH INSTITUTE CA $290,858
Gene Therapy NINDS 5R01NS054120-03 A Novel Orally Administered Macrophage Delivered Gene Therapy for Gaucher Disease GINNS, EDWARD UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $319,521
Gene Therapy NHLBI 5R01HL056205-12 Gene Transfer and Myocardial Function KOCH, WALTER THOMAS JEFFERSON UNIVERSITY PA $295,832
Gene Therapy NHLBI 5R01HL086741-02 Genetic Engineering of Vein Bypass Grafts in Vascular and Cardiovascular Surgery LOGERFO, FRANK BETH ISRAEL DEACONESS MEDICAL CENTER MA $509,665
Gene Therapy NCI 5R21CA115568-02 Design of targeted cell vehicles to ovarian carcinoma PEREBOEVA, LARISA UNIVERSITY OF ALABAMA AT BIRMINGHAM AL $174,600
Gene Therapy NIGMS 5R01GM070837-04 Integration of Murine Retroviral Vectors ROTH, MONICA UNIV OF MED/DENT NJ-R W JOHNSON MED SCH NJ $208,999
Gene Therapy NIAID 5R01AI056310-05 Adeno-associated Virus RNA Splicing and Polyadenylation PINTEL, DAVID UNIVERSITY OF MISSOURI-COLUMBIA MO $272,302
Gene Therapy NHLBI 5K08HL072865-06 Gene Therapy for the Wiskott Aldrich Syndrome STROM, TED UNIVERSITY OF TENNESSEE HEALTH SCI CTR TN $108,000
Gene Therapy NIDDK 5R01DK069705-04 E coli-based vectors for BAC delivery to mammalian cells WARBURTON, PETER MOUNT SINAI SCHOOL OF MEDICINE OF NYU NY $274,363
Gene Therapy NINDS 5R21NS054143-02 Targeted Toxin for Brain Cancer Gene Therapy CASTRO, MARIA CEDARS-SINAI MEDICAL CENTER CA $208,688
Gene Therapy NEI 5R01EY010804-13 SETTING THE STAGE FOR REPLACEMENT OF MITOCHONDRIAL GENES MORAES, CARLOS UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $419,045
Gene Therapy NCI 5R01CA076183-06 Targeting diffuse liver metastases with Herpes virus TANABE, KENNETH MASSACHUSETTS GENERAL HOSPITAL MA $375,113
Gene Therapy NIAID 5R01AI051388-05 AAV Vector Targeting Strategies for Gene Therapy BARTLETT, JEFFREY RESEARCH INST NATIONWIDE CHILDREN'S HOSP OH $283,700
Gene Therapy NIAID 5R21AI069018-02 Induction of Immunological Tolerance for Gene Therapy ZIMRING, JAMES EMORY UNIVERSITY GA $225,140
Gene Therapy NINDS 5R21NS058541-02 Global, Cell Type Specific Modulation of Selected Glutamate Transporters POULSEN, DAVID UNIVERSITY OF MONTANA MT $154,766
Gene Therapy NCI 5R01CA105171-05 Combining Virotherapy and Immunotherapy for Cancer KASAHARA, NORIYUKI UNIVERSITY OF CALIFORNIA LOS ANGELES CA $300,313
Gene Therapy NINDS 5R01NS053912-03 Intrabodies as novel neurological therapeutics MESSER, ANNE WADSWORTH CENTER NY $317,687
Gene Therapy NIAID 5R01AI068978-03 Targeting lentiviruses to infect chosen cells WANG, PIN UNIVERSITY OF SOUTHERN CALIFORNIA CA $574,827
Gene Therapy NIBIB 5R01EB004657-04 Design of Gene Delivery System to Target Hepatocytes DAVIS, MARK CALIFORNIA INSTITUTE OF TECHNOLOGY CA $378,593
Gene Therapy NHLBI 1R01HL087836-01A1 In vivo function and tolerance to Factor VIII variants LEE, BRENDAN BAYLOR COLLEGE OF MEDICINE TX $383,750
Gene Therapy NIBIB 5R21EB005331-02 Human Copper Transporter 1 as Reporter Gene for Imaging PENG, FANGYU WAYNE STATE UNIVERSITY MI $184,363
Gene Therapy NINDS 5R01NS054193-02 Gene Therapy and the Brain: Neuroimmune Interactions LOWENSTEIN, PEDRO CEDARS-SINAI MEDICAL CENTER CA $313,031
Gene Therapy NIGMS 5R01GM073901-03 Mechanisms of the AAV2 Rep motor protein LINDEN, R MOUNT SINAI SCHOOL OF MEDICINE OF NYU NY $317,236
Gene Therapy NCI 5R01CA108585-03 Armed Replicating Ad for Breast Cancer Bone Metastasis DOUGLAS, JOANNE UNIVERSITY OF ALABAMA AT BIRMINGHAM AL $225,695
Gene Therapy NHLBI 1R01HL090765-01 HSC transduction in situ by cellular delivery of integrating viral vectors KURRE, PETER OREGON HEALTH AND SCIENCE UNIVERSITY OR $380,680
Gene Therapy NHLBI 1R01HL090921-01 Cell selection strategies for the gene therapy of the beta-hemoglobinopathies LEBOULCH, PHILIPPE BRIGHAM AND WOMEN'S HOSPITAL MA $424,226
Gene Therapy NEI 1R01EY018656-01 Compacted DNA Nanoparticles for Ocular Therapy NAASH, MUNA UNIVERSITY OF OKLAHOMA HLTH SCIENCES CTR OK $366,250
Gene Therapy NIAID 1R01AI076652-01 Cloning major genes for lethal GVHD in mice CAO, THAI UNIVERSITY OF UTAH UT $299,833
Gene Therapy NCI 5R01CA107070-05 RGD-Polymer Targeting Plasmid to Angiogenic Endothelium KIM, SUNG WAN UNIVERSITY OF UTAH UT $261,534
Gene Therapy NEI 1R24EY018600-01 Leber Hereditary Optic Neuropathy: Gene Therapy Trial GUY, JOHN UNIVERSITY OF FLORIDA FL $871,453
Gene Therapy NICHD 5R01HD052682-02 Control of Breathing & Glycogen Storage Disease FULLER, DAVID UNIVERSITY OF FLORIDA FL $305,086
Gene Therapy NCI 5R01CA110176-04 Nonhuman adenoviral vectors for gene therapy MITTAL, SURESH PURDUE UNIVERSITY WEST LAFAYETTE IN $223,763
Gene Therapy NIBIB 1R21EB007208-01A2 Novel gene delivery and expression system LI, SHULIN LOUISIANA STATE UNIV A&M COL BATON ROUGE LA $183,750
Gene Therapy NCI 5R21CA122693-02 PET-guided Intervention in Lymphatic Metastasis of Prostate Cancer WU, LILY UNIVERSITY OF CALIFORNIA LOS ANGELES CA $185,400
Gene Therapy NINDS 5R01NS053540-03 Non-Viral Gene Targeting to the Brain PARDRIDGE, WILLIAM UNIVERSITY OF CALIFORNIA LOS ANGELES CA $303,790
Gene Therapy NINDS 5R01NS032677-16 Genetically Engineered Viruses for Brain Tumor Therapy MARTUZA, ROBERT MASSACHUSETTS GENERAL HOSPITAL MA $376,250
Gene Therapy NCI 1R21CA131774-01 Small RNA targeted gene activation for the treatment of prostate cancer LI, LONG-CHENG UNIVERSITY OF CALIFORNIA SAN FRANCISCO CA $208,238
Gene Therapy NIAID 2R01AI051390-07A1 Immunology of Factor IX Gene Transfer to Liver HERZOG, ROLAND UNIVERSITY OF FLORIDA FL $325,028
Gene Therapy NIDDK 1R01DK080477-01 ORAL GENE THERAPY WITH NiMOS FOR INFLAMMATORY BOWEL DISEASE AMIJI, MANSOOR NORTHEASTERN UNIVERSITY MA $333,625
Gene Therapy NCI 1R21CA132033-01 Targeted polymeric nanocarriers for combination therapy of prostate cancer FORREST, MARCUS UNIVERSITY OF KANSAS LAWRENCE KS $164,470
Gene Therapy NCI 5R01CA114340-02 Antiangiogenic Gene Therapy of Ovarian and Breast Cancers RAMAKRISHNAN, SUNDARAM UNIVERSITY OF MINNESOTA TWIN CITIES MN $253,417
Gene Therapy NCI 1R01CA132091-01 Targeted Nanoparticle DNA Therapy for Ovarian Cancer SAWICKI, JANET LANKENAU INSTITUTE FOR MEDICAL RESEARCH PA $304,559
Gene Therapy NINDS 5R21NS052432-02 Viral vector-based RNAi therapy for Alexander Disease BONTHIUS, DANIEL UNIVERSITY OF IOWA IA $193,594
Gene Therapy NCI 5R01CA107268-05 Pharmacology of Targeted Therapy to Brain Tumors SZOKA, FRANCIS UNIVERSITY OF CALIFORNIA SAN FRANCISCO CA $364,513
Gene Therapy NINDS 5K08NS046012-05 Intrathecal Gene Transfer for Chronic Cancer Pain BEUTLER, ANDREAS MOUNT SINAI SCHOOL OF MEDICINE OF NYU NY $168,291
Gene Therapy NCI 5R01CA102218-05 TRAIL-induced apoptosis in prostate cancer VOELKEL-JOHNSON, CHRISTINA MEDICAL UNIVERSITY OF SOUTH CAROLINA SC $249,182
Gene Therapy NIDDK 1R01DK077703-01A1 REDUCIBLE POLYAMIDO ETHYLENIMINE FOR GLP-1 PLASMID DELIVERY KIM, SUNG WAN UNIVERSITY OF UTAH UT $262,501
Gene Therapy NIDCR 5R01DE013397-08 Gene Therapy for Reconstructing Periodontal Tissues GIANNOBILE, WILLIAM UNIVERSITY OF MICHIGAN AT ANN ARBOR MI $403,105
Gene Therapy NCI 5R01CA081140-11 Model for Gene Therapy in X-linked Agammaglobulinemia RAWLINGS, DAVID CHILDREN'S HOSPITAL AND REG MEDICAL CTR WA $297,611
Gene Therapy NIGMS 5R01GM051449-12 Cutaneous Wound Repair with Transgenic Skin Cells in Pig ERIKSSON, ELOF BRIGHAM AND WOMEN'S HOSPITAL MA $372,207
Gene Therapy NINDS 5R21NS054989-02 RNAi Gene Silencing of alpha-Synuclein for Parkinson's Disease BOHN, MARTHA CHILDREN'S MEMORIAL HOSPITAL (CHICAGO) IL $160,781
Gene Therapy NIDDK 5R44DK064469-03 A new hepatocyte-specific ligand for gene delivery WONG, SO MIRUS BIO CORPORATION WI $617,364
Gene Therapy NHLBI 5R01HL078836-04 Evaluation of vectors based on group B adenoviruses LIEBER, ANDRE UNIVERSITY OF WASHINGTON WA $283,183
Gene Therapy NIDDK 5R01DK068343-03 Mechanism of B-cell Delivered Tolerance in Diabetes SCOTT, DAVID UNIVERSITY OF MARYLAND BALTIMORE MD $311,976
Gene Therapy NIMH 1R21MH082421-01 HSV amplicon vectors for neuroscience research CHIOCCA, E. ANTONIO OHIO STATE UNIVERSITY OH $202,500
Gene Therapy NCI 1R01CA122930-01A2 Conditionally Replicative Adenoviral Vectors for Malignant Glioma LESNIAK, MACIEJ UNIVERSITY OF CHICAGO IL $323,817
Gene Therapy NIAID 5R01AI033657-14 Baculovirus envelope proteins and insect cells BLISSARD, GARY BOYCE THOMPSON INST FOR PLANT RESEARCH NY $204,939
Gene Therapy NHLBI 1R01HL084381-01A2 Molecular engineering of factor VIII gene for rAAV delivery XIAO, WEIDONG CHILDREN'S HOSPITAL OF PHILADELPHIA PA $364,302
Gene Therapy NIAID 5R01AI058697-04 Overcoming HIV-1 resistance to RNA Interference RAMRATNAM, BHARAT RHODE ISLAND HOSPITAL (PROVIDENCE, RI) RI $347,418
Gene Therapy NIDDK 2R01DK038795-20A2 Krabbe disease: Combined therapies for the central and peripheral nervous systems WENGER, DAVID THOMAS JEFFERSON UNIVERSITY PA $309,333
Gene Therapy NINDS 2R01NS035633-10A2 Gene Therapy and Seizures MCCOWN, THOMAS UNIVERSITY OF NORTH CAROLINA CHAPEL HILL NC $316,867
Gene Therapy NIAID 1R01AI072176-01A1 Rational and combinatorial engineering of AAV vectors SAMULSKI, RICHARD UNIVERSITY OF NORTH CAROLINA CHAPEL HILL NC $373,669
Gene Therapy NIAID 5R01AI042552-11 Combinatorial Use of Anti-HIV RNA-based Therapeutics ROSSI, JOHN CITY OF HOPE/BECKMAN RESEARCH INSTITUTE CA $377,840
Gene Therapy NIAID 5K25AI058672-05 Multiscale studies of HIV infection and treatment CHOU, TOM UNIVERSITY OF CALIFORNIA LOS ANGELES CA $126,886
Gene Therapy NHLBI 1R01HL088426-01A1 Translational Studies of AAV Gene Transfer for CHF HAMMOND, H KIRK VETERANS MEDICAL RESEARCH FDN/SAN DIEGO CA $346,250
Gene Therapy NEI 2R01EY012155-11 Deactivation of Visual Pigments in vivo CHEN, JEANNIE UNIVERSITY OF SOUTHERN CALIFORNIA CA $649,278
Gene Therapy NIA 1R01AG030048-01A1 A Phase 2 Trial of AAV-NGF Gene Delivery in Alzheimer's Disease AISEN, PAUL UNIVERSITY OF CALIFORNIA SAN DIEGO CA $2,095,517
Gene Therapy NHLBI 5R01HL053670-14 Lentiviral Vectors for Gene Transfer VERMA, INDER SALK INSTITUTE FOR BIOLOGICAL STUDIES CA $635,999
Gene Therapy NHLBI 5R01HL064274-08 Hepatic Gene Transfer for Treatment of Hemophilias A&B KAY, MARK STANFORD UNIVERSITY CA $513,056
Gene Therapy NCI 5R01CA121258-02 Cellular Transduction with Replication-Competent Retrovirus Vectors KASAHARA, NORIYUKI UNIVERSITY OF CALIFORNIA LOS ANGELES CA $467,899
Gene Therapy NINDS 5F32NS054453-02 Targeting Therapeutic Gene Vectors to Reactive Glia XU, JIANFENG BETH ISRAEL DEACONESS MEDICAL CENTER MA $58,036
Gene Therapy NINDS 5R01NS053559-03 Pathogenesis and possible therapies modelled in ovine Batten disease PALMER, DAVID LINCOLN UNIVERSITY NEW ZE $268,384
Gene Therapy NINDS 2R01NS045855-05A1 Promoters for Long-term Expression from HSV-1 Vectors GELLER, ALFRED HARVARD UNIVERSITY (MEDICAL SCHOOL) MA $253,378
Gene Therapy NEI 5R01EY005951-22 Oxidative damage and cone cell death in RP CAMPOCHIARO, PETER JOHNS HOPKINS UNIVERSITY MD $508,409
Gene Therapy NEI 5R01EY016861-02 Exploring plasticity of the adult visual system using viral gene delivery NEITZ, MAUREEN MEDICAL COLLEGE OF WISCONSIN WI $371,175
Gene Therapy NIDDK 5R01DK042716-16 Protection from GVHD with Gene-Modified Donor T Cells NASH, RICHARD FRED HUTCHINSON CANCER RESEARCH CENTER WA $377,773
Gene Therapy NINDS 5R21NS053770-02 Silencing mutant SOD1 in vivo for treatment of ALS XU, ZUOSHANG UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $178,403
Gene Therapy NIDDK 5R01DK056845-09 Establishment and maintenance of repressed chromatin BOUHASSIRA, ERIC YESHIVA UNIVERSITY NY $363,163
Gene Therapy NIAID 5R01AI057066-05 SiRNA Gene Therapy for HIV/AIDS AKKINA, RAMESH COLORADO STATE UNIVERSITY-FORT COLLINS CO $303,468
Gene Therapy NHLBI 5R01HL077421-04 Stem Cell Therapy for Pulmonary Hypertension KADOWITZ, PHILIP TULANE UNIVERSITY OF LOUISIANA LA $413,096
Gene Therapy NCI 5R01CA080192-09 ONCOLYTIC ADENOVIRUSES FOR CERVICAL CANCER GENE THERAPY LIEBER, ANDRE UNIVERSITY OF WASHINGTON WA $226,398
Gene Therapy NEI 5R01EY001919-32 Cellular Mechanisms of Inherited Retinal Degeneration LAVAIL, MATTHEW UNIVERSITY OF CALIFORNIA SAN FRANCISCO CA $634,272
Gene Therapy NEI 5R01EY011731-11 Rhodopsin Gene Correction and Gene Knockout in Rod Cells WILSON, JOHN BAYLOR COLLEGE OF MEDICINE TX $402,085
Gene Therapy NEI 5K08EY017024-03 non-viral medicated gene targeting to the retina CHUNG, DANIEL UNIVERSITY OF PENNSYLVANIA PA $145,025
Gene Therapy NCI 5R01CA119298-03 Glioma Therapy Using Targeted Oncolytic HSV Vectors GLORIOSO, JOSEPH UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $349,393
Gene Therapy NINDS 1R21NS054768-01A2 Gene therapy for Ataxia Telangiectasia CORTES, MARIA MASSACHUSETTS GENERAL HOSPITAL MA $210,300
Gene Therapy NCI 5R01CA120327-02 Molecular Imaging of Cancer In vivo via Targeted Transduction CHEN, IRVIN UNIVERSITY OF CALIFORNIA LOS ANGELES CA $234,840
Gene Therapy NEI 5R01EY017294-02 Gene therapy in the cornea MOHAN, RAJIV UNIVERSITY OF MISSOURI-COLUMBIA MO $329,082
Gene Therapy NIAMS 5R01AR049537-06 Altered Matrix-Cells and Intermolecular Interactions FERTALA, ANDRZEJ THOMAS JEFFERSON UNIVERSITY PA $338,358
Gene Therapy NIAID 5R01AI064344-04 MODULATION OF REGULATORY TOLERANCE TO TRANSPLANTS LEGUERN, CHRISTIAN MASSACHUSETTS GENERAL HOSPITAL MA $515,180
Gene Therapy NHLBI 4R37HL033610-23 Brain Angiotensin In Hypertensive Neurons in Culture RAIZADA, MOHAN UNIVERSITY OF FLORIDA FL $686,851
Gene Therapy NIMH 5R01MH070287-05 Targeting HIV infection of the cns using gene delivery STRAYER, DAVID THOMAS JEFFERSON UNIVERSITY PA $372,161
Gene Therapy NIAID 5R01AI069350-03 Retargeting of Retroviral Vectors CHEN, IRVIN UNIVERSITY OF CALIFORNIA LOS ANGELES CA $341,020
Gene Therapy NCI 5R01CA109446-05 Recombinant Immunotherapy for Renal Cell Carcinoma GRIFFITH, THOMAS UNIVERSITY OF IOWA IA $258,035
Gene Therapy NIDDK 5K01DK063992-05 Gene therapy for Cooley's anemia in a new mouse model RIVELLA, STEFANO WEILL MEDICAL COLLEGE OF CORNELL UNIV NY $129,133
Gene Therapy NIDDK 5R01DK072537-03 Tolerance Induction by Neonatal Gene Delivery GAENSLER, KARIN UNIVERSITY OF CALIFORNIA SAN FRANCISCO CA $301,145
Gene Therapy NCI 5R21CA125327-02 Nanoscale Functional Dendrimer-DNA Assemblies GRINSTAFF, MARK BOSTON UNIVERSITY MA $162,500
Gene Therapy NIDDK 5R01DK059371-05 AAV2/8 vector-mediated liver gene therapy for phenylketonuria (PKU) HARDING, CARY OREGON HEALTH AND SCIENCE UNIVERSITY OR $279,677
Gene Therapy NIAID 5R01AI074043-02 In Vivo ADA Gene Delivery for the Treatment of SCID KOHN, DONALD CHILDREN'S HOSPITAL LOS ANGELES CA $483,204
Gene Therapy NIDDK 5R01DK055759-10 Gene Targeting by Adeno-Associated Virus Vectors RUSSELL, DAVID UNIVERSITY OF WASHINGTON WA $309,913
Gene Therapy NIDDK 5R01DK066212-04 Proteosome Inhibitor Enhanced Non-Viral Gene Delivery RICE, KEVIN UNIVERSITY OF IOWA IA $250,387
Gene Therapy NCI 5R01CA104873-05 HPV helper functions for AAV Replication HERMONAT, PAUL UNIVERSITY OF ARKANSAS MED SCIS LTL ROCK AR $227,407
Gene Therapy NHLBI 5R01HL076901-06 Human Parvovirus B19 Vectors: Mechanism of Transduction SRIVASTAVA, ARUN UNIVERSITY OF FLORIDA FL $344,900
Gene Therapy NIDDK 5R01DK058702-07 Episomal lenti vector for a humanized hemophilia mouse KAFRI, TAL UNIVERSITY OF NORTH CAROLINA CHAPEL HILL NC $262,949
Gene Therapy NHLBI 5R01HL081148-04 Alveolar Epithelial Cell-Specific Gene Therapy Plasmids DEAN, DAVID UNIVERSITY OF ROCHESTER NY $373,835
Gene Therapy NHLBI 5R01HL083047-02 Aerosol delivery of HDAd into Primate Lungs: Preclinical CF Gene Therapy Studies NG, PHILIP BAYLOR COLLEGE OF MEDICINE TX $704,125
Gene Therapy NCI 5R21CA122213-02 Novel oncolytic adenovirus for pancreatic therapy KIM, BAEK UNIVERSITY OF ROCHESTER NY $215,600
Gene Therapy NIAMS 5R37AR040864-19 Dystrophin Replacement in mdx mice CHAMBERLAIN, JEFFREY UNIVERSITY OF WASHINGTON WA $504,779
Gene Therapy NINDS 5R01NS038690-07 AAV Gene Therapy for the CNS in MPS VII WOLFE, JOHN CHILDREN'S HOSPITAL OF PHILADELPHIA PA $446,473
Gene Therapy NCI 5R01CA125272-02 Cellular co-factors in stable retroviral transduction DANIEL, RENE THOMAS JEFFERSON UNIVERSITY PA $235,600
Gene Therapy NIAID 5R01AI065429-04 Innate immunity to adenovirus vectors SHAYAKHMETOV, DMITRY UNIVERSITY OF WASHINGTON WA $282,026
Gene Therapy NIDDK 1R41DK076516-01A2 A novel approach for gene therapy MAAS, STEFAN ATIGEN PA $139,916
Gene Therapy NCI 1R43CA128278-01A1 Functional Vectors for Treatment of Mesothelioma BALABAI, NATALIA FIFTH BASE, LLC FL $165,920
Gene Therapy NHLBI 1R13HL091555-01 2008 Viral Vectors for Gene Therapy, The Science of Gordon Research Conference ROBBINS, PAUL GORDON RESEARCH CONFERENCES RI $15,000
Gene Therapy NIDDK 5R01DK065656-05 CARP: Angiogenic Gene Therapy in Diabetic Wounds DAVIDSON, JEFFREY VANDERBILT UNIVERSITY TN $283,068
Gene Therapy NCI 5R01CA049248-19 Hepatic Metabolism of Anti-cancer Drugs WAXMAN, DAVID BOSTON UNIVERSITY MA $275,637
Gene Therapy NIDDK 5R01DK061408-07 HGF Gene Therapy for Chronic Renal Fibrosis LIU, YOUHUA UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $258,446
Gene Therapy NHLBI 5R01HL083017-02 Preclinical gene correction of hemophilia A KAZAZIAN, HAIG UNIVERSITY OF PENNSYLVANIA PA $395,386
Gene Therapy NCI 5R01CA109711-04 Gene Delivery Modulated by Redox Potential Gradients OUPICKY, DAVID WAYNE STATE UNIVERSITY MI $249,211
Gene Therapy NCI 5R21CA116014-02 A NOVEL TARGETED THERAPEUTIC USING VIRAL CAPSID PROTEIN MEDINA-KAUWE, LALI CEDARS-SINAI MEDICAL CENTER CA $190,800
Gene Therapy NIDDK 5R01DK068399-03 Non-viral Liver-targeted Gene Delivery MAO, HAI-QUAN JOHNS HOPKINS UNIVERSITY MD $283,668
Gene Therapy NIA 2R42AG026174-02A2 Cell-Based, Chronic Wound Gene Therapy for Older Adults ALLEN-HOFFMANN, LYNN STRATATECH CORPORATION WI $401,433
Gene Therapy NINDS 5R01NS055143-02 TH and GTPCHI gene therapy for Parkinson's disease KORDOWER, JEFFREY RUSH UNIVERSITY MEDICAL CENTER IL $465,614
Gene Therapy NEI 5R01EY010581-12 Therapies for Photoreceptor Degeneration LI, TIANSEN MASSACHUSETTS EYE AND EAR INFIRMARY MA $179,611
Gene Therapy NHLBI 1R43HL086213-01A1 Facilitation of Autologous Hematopoietic Stem Cell Engraftment for Gene Therapy DOWN, JULIAN GENETIX PHARMACEUTICALS, INC. MA $249,705
Gene Therapy NCI 5R01CA070337-12 Combination gene therapy for metastatic colon cancer CHEN, SHU-HSIA MOUNT SINAI SCHOOL OF MEDICINE OF NYU NY $287,106
Gene Therapy NHLBI 7R01HL081499-03 Novel Molecular and Cellular Therapies in Fanconi Anemia WILLIAMS, DAVID CHILDREN'S HOSPITAL BOSTON MA $325,790
Gene Therapy NCI 5R01CA060999-13 pRb2/p130: from the mechanisms to gene therapy GIORDANO, ANTONIO TEMPLE UNIVERSITY PA $321,078
Gene Therapy NINDS 5K08NS046430-04 Targeted Adenoviral Gene Therapy for Malignant Glioma LESNIAK, MACIEJ UNIVERSITY OF CHICAGO IL $165,078
Gene Therapy NIDA 1R43DA023374-01A1 Chronic pain therapy through upregulation of opioid receptors WANG, CONGYING MAJESTECK BIOSCIENCE TX $219,917
Gene Therapy NCI 2P01CA094237-06 9002 VECTOR PRODUCTION GEE, ADRIAN BAYLOR COLLEGE OF MEDICINE TX $294,859
Gene Therapy NHLBI 5R13HL072168-07 Annual Gene Therapy Symposium for Heart, Lung, and Blood Diseases TARANTAL, ALICE UNIVERSITY OF CALIFORNIA DAVIS CA $10,000
Gene Therapy NIAID 5R13HL072168-07 Annual Gene Therapy Symposium for Heart, Lung, and Blood Diseases TARANTAL, ALICE UNIVERSITY OF CALIFORNIA DAVIS CA $5,000
Gene Therapy NIBIB 5R13HL072168-07 Annual Gene Therapy Symposium for Heart, Lung, and Blood Diseases TARANTAL, ALICE UNIVERSITY OF CALIFORNIA DAVIS CA $3,000
Gene Therapy NCI 5R01CA092487-05 Oncolytic adenovector-mediated TRAIL gene therapy for cancers FANG, BINGLIANG UNIVERSITY OF TEXAS MD ANDERSON CAN CTR TX $314,553
Gene Therapy NIAMS 5R21AR055712-02 Muscle-specific AAV Vectors for DMD Gene Therapy SAMULSKI, RICHARD UNIVERSITY OF NORTH CAROLINA CHAPEL HILL NC $153,811
Gene Therapy NINDS 1F31NS059283-01A1 Targeting Amyloid Beta Oligomers in the 3xTg-AD Mouse Model with scFv Antibodies RYAN, DEBORAH UNIVERSITY OF ROCHESTER NY $40,972
Gene Therapy NCI 7R01CA107621-04 Engineering Polymers For Gene Therapy of Head Cancer SWAAN, PETER UNIVERSITY OF UTAH UT $281,835
Gene Therapy NEI 5R01EY016470-03 Gene Delivery in Retinal Diseases NICKERSON, JOHN EMORY UNIVERSITY GA $327,582
Gene Therapy NIAID 5R01AI043619-11 Tolerance to allografts through gene therapy IACOMINI, JOHN BRIGHAM AND WOMEN'S HOSPITAL MA $300,442
Gene Therapy NINDS 1F31NS056780-01A2 Inducing Tolerance to Gene Transfer in Dystrophic Mice EGHTESAD, SAMAN UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $40,972
Gene Therapy NINDS 2P01NS040923-06A1 0006 Vector delivery to modify the brain tumor and its microenvironment GLORIOSO, JOSEPH UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $273,580
Gene Therapy NIGMS 1F32GM083594-01 Gene correction in hematopoitic stem cells using a retargetable meganuclease VOLLES, MICHAEL HARVARD UNIVERSITY (MEDICAL SCHOOL) MA $52,898
Gene Therapy NCI 5R01CA100893-05 Use of Adjuvants to Improve Skin Genetic Immunizations LARREGINA, ADRIANA UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $256,287
Gene Therapy NCI 5R01CA107082-04 T Cell Based Carriers for In Vivo Gene Therapy of Cancer VILE, RICHARD MAYO CLINIC COLL OF MEDICINE, ROCHESTER MN $279,026
Gene Therapy NEI 1F31EY018082-01A2 Signal transduction pathways involved in adult cortical plasticity PENA, JOHN WEILL MEDICAL COLLEGE OF CORNELL UNIV NY $49,681
Gene Therapy NIDCR 5R01DE013386-07 COMBINATORIAL GENE THERAPY FOR BONE REGENERATION FRANCESCHI, RENNY UNIVERSITY OF MICHIGAN AT ANN ARBOR MI $325,604
Gene Therapy NHLBI 5R44HL076908-03 Transposon-Mediated Gene Therapy for Fanconi Anemia MCIVOR, R DISCOVERY GENOMICS, INC. MN $566,484
Gene Therapy NHLBI 5R01HL073838-04 rAAV-Mediated Gene Therapy for Hemophillia B DAVIDOFF, ANDREW ST. JUDE CHILDREN'S RESEARCH HOSPITAL TN $355,568
Gene Therapy NCI 5R01CA116621-04 Her2-targeted vectors for gene therapy of cancer KRASNYKH, VICTOR UNIVERSITY OF TEXAS MD ANDERSON CAN CTR TX $322,144
Gene Therapy NCI 5R01CA106298-05 Imbalancing DNA BER to enhance Ovarian Tumor Sensitivity KELLEY, MARK INDIANA UNIV-PURDUE UNIV AT INDIANAPOLIS IN $285,864
Gene Therapy NCI 5R01CA111569-04 Capsid-labeled adenovirus for virotherapy monitoring CURIEL, DAVID UNIVERSITY OF ALABAMA AT BIRMINGHAM AL $262,662
Gene Therapy NCI 5R01CA085939-09 Improving Suicide Genes for Cancer Gene Therapy BLACK, MARGARET WASHINGTON STATE UNIVERSITY WA $263,260
Gene Therapy NIAMS 5R01AR050595-06 Gene Therapy for a severe DMD Animal Model XIAO, XIAO UNIVERSITY OF NORTH CAROLINA CHAPEL HILL NC $297,689
Gene Therapy NCI 5R01CA113662-04 DNA Damage Targeted Gene Therapy in Head & Neck Cancer WEICHSELBAUM, RALPH UNIVERSITY OF CHICAGO IL $263,390
Gene Therapy NHLBI 5R01HL088467-02 Safe, Silencing-Resistant, Non-Oncogenic Globin Expression Cassettes BOUHASSIRA, ERIC YESHIVA UNIVERSITY NY $477,970
Gene Therapy NCI 5R01CA089325-07 Regulation of Targeted Gene Correction KMIEC, ERIC UNIVERSITY OF DELAWARE DE $210,384
Gene Therapy NEI 5R01EY014026-05 Oligonucleotide Repair of a Retinal Degeneration Model BOATRIGHT, JEFFREY EMORY UNIVERSITY GA $363,992
Gene Therapy NEI 5R01EY009357-14 Vasculogenesis and hyperoxia in the developing retina. LUTTY, GERARD JOHNS HOPKINS UNIVERSITY MD $312,118
Gene Therapy NIBIB 5R01EB005658-03 Reversing Electrostatic Interactions for Improved Gene Delivery GRINSTAFF, MARK BOSTON UNIVERSITY MA $336,476
Gene Therapy NIBIB 5R21EB006520-02 Parallel gene delivery from spinal cord bridges SHEA, LONNIE NORTHWESTERN UNIVERSITY IL $173,588
Gene Therapy NCI 5R01CA118022-03 Hamster Model for Oncolytic Adenovirus Vectors WOLD, WILLIAM SAINT LOUIS UNIVERSITY MO $253,359
Gene Therapy NCI 5R01CA102139-05 Genetically Engineered Viruses for Prostate Cancer Therapy MARTUZA, ROBERT MASSACHUSETTS GENERAL HOSPITAL MA $340,161
Gene Therapy NIDDK 5R01DK069968-04 Growth Factor and Antiapoptotic Gene Delivery to Human Islets MAHATO, RAM UNIVERSITY OF TENNESSEE HEALTH SCI CTR TN $238,771
Gene Therapy FIC 1R01AG029798-01A1 Neuroprotective Gene Therapy in the Brain of Senile Rats GOYA, RODOLFO NATIONAL UNIVERSITY OF LA PLATA ARGENT $25,000
Gene Therapy NIA 1R01AG029798-01A1 Neuroprotective Gene Therapy in the Brain of Senile Rats GOYA, RODOLFO NATIONAL UNIVERSITY OF LA PLATA ARGENT $130,975
Gene Therapy NIDDK 5R01DK053244-12 Molecular Remedy of Mitochondrial Defects YAGI, TAKAO SCRIPPS RESEARCH INSTITUTE CA $331,043
Gene Therapy NIDDK 5R01DK058318-09 Accessing the Airway for Cystic Fibrosis Gene Therapy DAVIS, PAMELA CASE WESTERN RESERVE UNIVERSITY OH $334,100
Gene Therapy NHLBI 5R01HL083078-02 Translational studies in Heart Failure Gene Therapy BRIDGES, CHARLES UNIVERSITY OF PENNSYLVANIA PA $727,681
Gene Therapy NIA 5R01AG025509-04 AAV Gene Therapy for Alzheimer's Disease MORGAN, DAVID UNIVERSITY OF SOUTH FLORIDA FL $408,989
Gene Therapy NIAID 5R01AI073255-02 Humanized Rag2-/-gammac-/-mice for HIV infection and gene therapy AKKINA, RAMESH COLORADO STATE UNIVERSITY-FORT COLLINS CO $360,518
Gene Therapy NCI 5R01CA116322-02 Tumor and PTK-Targeted Therapy by FUS1 and PTK inhibitor JI, LIN UNIVERSITY OF TEXAS MD ANDERSON CAN CTR TX $292,600
Gene Therapy NINDS 5R21NS059518-02 Directed Evolution of Adeno-Associated Virus Vectors for Seizure Gene Therapy MCCOWN, THOMAS UNIVERSITY OF NORTH CAROLINA CHAPEL HILL NC $157,404
Gene Therapy NHLBI 1R21HL091808-01 Allele-Specific Repair of the CFTR DeltaF508 Mutation using Zinc Finger Nucleases MCCRAY, PAUL UNIVERSITY OF IOWA IA $215,500
Gene Therapy NCI 5R01CA074042-11 Tissue Specific Gene Therapy for Human Prostate Cancer KAO, CHINGHAI INDIANA UNIV-PURDUE UNIV AT INDIANAPOLIS IN $265,033
Gene Therapy NCI 5R01CA116591-03 Polymer Based Gene Delivery KABANOV, ALEXANDER UNIVERSITY OF NEBRASKA MEDICAL CENTER NE $260,726
Gene Therapy NINDS 5R01NS051644-03 Ischemic Spasticity: Modulation by GAD65 Gene Delivery MARSALA, MARTIN UNIVERSITY OF CALIFORNIA SAN DIEGO CA $337,544
Gene Therapy NCI 5U01CA084306-10 Investigation of lung tumor development and treatment JACKS, TYLER MASSACHUSETTS INSTITUTE OF TECHNOLOGY MA $870,330
Gene Therapy NEI 5R24EY017540-02 Adult Stem Cells for Therapy of Visual Disorders FRIEDLANDER, MARTIN SCRIPPS RESEARCH INSTITUTE CA $3,346,543
Gene Therapy NCI 5R01CA107492-04 Prevention of insertional mutagenesis in gene therapy BAUM, CHRISTOPHER CHILDREN'S HOSPITAL MED CTR (CINCINNATI) OH $224,720
Gene Therapy NCI 5K08CA103859-04 Image-guided Gene and Virotherapy for Pancreatic Cancer CARLSON, STEPHANIE MAYO CLINIC COLL OF MEDICINE, ROCHESTER MN $131,220
Gene Therapy NINDS 5R01NS057558-02 Targeted Gene Transfer, to Specific Types of Neurons, with HSV-1 Vectors GELLER, ALFRED HARVARD UNIVERSITY (MEDICAL SCHOOL) MA $253,378
Gene Therapy NCI 5R01CA122568-02 Ligand-Directed Tumor Targeting in Preclinical Models PASQUALINI, RENATA UNIVERSITY OF TEXAS MD ANDERSON CAN CTR TX $292,600
Gene Therapy NCI 5R01CA100830-06 Oncolytic VSV for Hepatocellular Carcinoma WOO, SAVIO MOUNT SINAI SCHOOL OF MEDICINE OF NYU NY $338,076
Gene Therapy NIDDK 5R01DK068216-04 COMPREHENSIVE GENE THERAPY FOR MUCOPOLYSACCHARIDOSIS VII ROY-CHOWDHURY, JAYANTA YESHIVA UNIVERSITY NY $324,718
Gene Therapy NIAID 5R01AI039126-14 Foamy Virus Vector for Immunodeficiency Viruses Therapy MERGIA, AYALEW UNIVERSITY OF FLORIDA FL $323,362
Gene Therapy NCI 5R01CA115527-02 Targeting Nanoparticle DNA Delivery to Prostate Tumors SAWICKI, JANET LANKENAU INSTITUTE FOR MEDICAL RESEARCH PA $310,762
Gene Therapy NIBIB 5R01EB004533-04 Somatostatin Receptor Based PET Imaging of Gene Transfer ROGERS, BUCK WASHINGTON UNIVERSITY MO $288,754
Gene Therapy NHLBI 5R01HL057619-11 Mouse Model of Sickle Cell Disease and Genetic Therapies TOWNES, TIM UNIVERSITY OF ALABAMA AT BIRMINGHAM AL $426,051
Gene Therapy NINDS 5R01NS044576-06 Somatic Cell Gene Transfer/Neurological & Clinical Applications DURING, MATTHEW OHIO STATE UNIVERSITY OH $329,559
Gene Therapy NIAMS 5K08AR049201-05 Gene Therapy for Cartilage Injury BERTONE, ALICIA OHIO STATE UNIVERSITY OH $124,713
Gene Therapy NHLBI 5R01HL085693-03 Gene therapy for Fanconi anemia KIEM, HANS-PETER FRED HUTCHINSON CANCER RESEARCH CENTER WA $638,503
Gene Therapy NIAMS 5R03AR054955-02 Adult muscle stem cells as cell therapy in utrophin-dystrophin deficient mice REYES, MORAYMA UNIVERSITY OF WASHINGTON WA $81,340
Gene Therapy NHLBI 5R13HL078311-05 Conference--American Society of Gene Therapy KOHN, DONALD AMERICAN SOCIETY OF GENE THERAPY WI $10,000
Gene Therapy NINDS 5R01NS041584-07 Determinants that regulate splicing of SMN LORSON, CHRISTIAN UNIVERSITY OF MISSOURI-COLUMBIA MO $326,620
Gene Therapy NCI 2P01CA094060-06A1 0001 Mouse Models for Tumor Progression and Maintenance VARMUS, HAROLD SLOAN-KETTERING INSTITUTE FOR CANCER RES NY $407,911
Gene Therapy NIDDK 5R01DK068134-03 Oxidative Stress and Vascular HO in Diabetes ABRAHAM, NADER NEW YORK MEDICAL COLLEGE NY $310,166
Gene Therapy NCRR 5K01RR019979-05 Neuropathology of a Mouse Model for Phenylketonuria EMBURY, JENNIFER UNIVERSITY OF FLORIDA FL $111,998
Gene Therapy NHLBI 5R01HL081527-02 Engineering AAV Vectors to Evade Antibody Neutralization SCHAFFER, DAVID UNIVERSITY OF CALIFORNIA BERKELEY CA $361,214
Gene Therapy NINDS 5R01NS055165-02 STEM/PROGENITOR CELL PROTECTION FOR PARKINSON'S DISEASE STEINDLER, DENNIS UNIVERSITY OF FLORIDA FL $317,742
Gene Therapy NHLBI 5R01HL065519-07 Molecular Chimerism Therapy for Hemophilia A HAWLEY, ROBERT GEORGE WASHINGTON UNIVERSITY DC $371,408
Gene Therapy NHLBI 5R01HL066565-08 Mechanisms of Cardiopulmonary Gene Transfer DIAMOND, SCOTT UNIVERSITY OF PENNSYLVANIA PA $314,579
Gene Therapy NIDCR 5K22DE015612-05 A Novel Herpesviral Vector for Oral Gene Delivery DENG, HONGYU UNIVERSITY OF CALIFORNIA LOS ANGELES CA $135,000
Gene Therapy NHLBI 5R01HL081582-04 Sleeping Beauty Gene Therapy from Liver to BOECs STEER, CLIFFORD UNIVERSITY OF MINNESOTA TWIN CITIES MN $354,382
Gene Therapy NCI 5R01CA109451-04 Gene Delivery Vehicles for Cancer Gene Therapy MARINI, FRANK UNIVERSITY OF TEXAS MD ANDERSON CAN CTR TX $183,473
Gene Therapy NIAMS 5R03AR054929-02 The study of gene therapy for aseptic loosening using a mouse implant model YANG, SHANG-YOU WAYNE STATE UNIVERSITY MI $73,745
Gene Therapy NCI 5R01CA081171-08 Viral Proteins: Gene Delivery to Specific Malignancies ALBRITTON, LORRAINE UNIVERSITY OF TENNESSEE HEALTH SCI CTR TN $249,183
Gene Therapy NIBIB 1R21EB008951-01 First-Principles, Computer-Aided Nanosystem Design and Analysis ORTOLEVA, PETER INDIANA UNIVERSITY BLOOMINGTON IN $269,500
Gene Therapy NINDS 5R21NS057556-02 Neurovascular Mechanisns of Brain Function and Disease LIU, PHILIP MASSACHUSETTS GENERAL HOSPITAL MA $190,837
Gene Therapy NIBIB 5R01EB005740-04 NOVEL MARKERS FOR IMAGING GENE EXPRESSION IN VIVO USING MRI AHRENS, ERIC CARNEGIE-MELLON UNIVERSITY PA $310,120
Gene Therapy NICHD 1P01HD057247-01 0001 Immune Barriers to AAV Gene Therapy WILSON, JAMES% UNIVERSITY OF PENNSYLVANIA PA $122,894
Gene Therapy NICHD 1P01HD057247-01 0002 Preclinical Studies of AAV Gene Therapy in MOuse Models of Urea Cycle Disorders WILSON, JAMES% UNIVERSITY OF PENNSYLVANIA PA $122,883
Gene Therapy NICHD 1P01HD057247-01 0003 Molecular Characterization of Liver Gene Transfer and Its Oncogenic Potential GAO, GUANG-PING% UNIVERSITY OF PENNSYLVANIA PA $122,883
Gene Therapy NICHD 1P01HD057247-01 9001 Vector Core JOHNSTON, JULIE% UNIVERSITY OF PENNSYLVANIA PA $122,883
Gene Therapy NICHD 1P01HD057247-01 9003 Animal Models Core HANKENSON, CLAIRE% UNIVERSITY OF PENNSYLVANIA PA $122,883
Gene Therapy NIBIB 5R01EB005441-03 Electroporation System for Cutaneous Gene Transfer HELLER, RICHARD UNIVERSITY OF SOUTH FLORIDA FL $315,300
Gene Therapy NIAID 5R37AI029329-20 Enhancing the Intracellular Functioning of anti-HIV RNAs ROSSI, JOHN CITY OF HOPE/BECKMAN RESEARCH INSTITUTE CA $645,362
Gene Therapy NHLBI 5R01HL077844-04 CFTR Delivery to Ciliated Airway Cells by PIV Vectors PICKLES, RAYMOND UNIVERSITY OF NORTH CAROLINA CHAPEL HILL NC $344,505
Gene Therapy NIAMS 5R01AR047981-08 Strategies Towards Gene Therapy for Dystrophic Epidermolysis Bullosa CHEN, MEI UNIVERSITY OF SOUTHERN CALIFORNIA CA $333,218
Gene Therapy NCI 5R01CA121153-02 Development of Highly Targeted, Imageable Adenoviral Vectors for Prostate Cancer RODRIGUEZ, RONALD JOHNS HOPKINS UNIVERSITY MD $311,600
Gene Therapy NINDS 5F31NS058224-02 Delivery of a Myostatin Inhibitor by AAV Gene Therapy for Muscular Dystrophy HAIDET, AMANDA RESEARCH INST NATIONWIDE CHILDREN'S HOSP OH $31,003
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